Gene Therapy is changing the world of genetic diseases.

Gene therapy targets the underlying cause of a disease and has the potential to replace the faulty NF2 gene with a healthy copy of the gene or to cause existing tumor cells to die off through a process called apoptosis.

Accelerating gene therapy to cure NF2


“I am highly optimistic that this gene therapy strategy can represent an effective and safe therapy for patients with schwannomas – whether associated with NF2, schwannomatosis or sporadic schwannomas”.

Gary J Brenner, MD, PhD, Associate Professor, Harvard Medical School. Director, Massachusetts General Hospital pain medicine fellowship

Message from Dr. Nicole Henwood, founder, and president of NF2 BioSolutions and mother of AJ diagnosed with NF2



What is Gene Replacement Therapy?

video provided courtesy of Avexis

Next Steps:

Our next steps include continuing to identify and sponsor leading gene, cell and novel therapy labs to investigate the different therapy approaches that were discussed at our March 2019 consortium in Boston. At the NF2 Gene Therapy Consortium, organized by NF2 BioSolutions, we had more than 40 biotech executives, researchers & clinicians from NF2 or leading Gene Therapy labs, all brainstorming on which novel therapy approaches could be applied on finding a cure for NF2.

To date, NF2 BioSolutions is collaborating with four labs and has set up an open access NF2 biobank to accelerate gene therapy research for NF2. Check out our research initiatives page.

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Volunteer:

NF2 BioSolutions was founded in July 2018 with the goal of fighting back against NF2 and we won’t stop until we save our children and ourselves! We need you to volunteer your time and/or donate to advance research studies to the next phase. Every dollar received in donations is carefully spent and put towards accelerating NF2 research. Check out our Board of Directors and Scientific Advisory Board.

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Contact Gil at gilles@nf2biosolutions.org to volunteer or to learn more about us.


Current fundraising status:


Our Mission:

Mission: We are a non-profit organization (Tax-ID 83-0940046) seeking a cure or preventative treatment for NF2 by vigorously supporting and advancing existing and next-generation biomedical technologies, such as gene therapy and immunotherapy.

Vision: We envision a world where those living with NF2 will have access to cutting-edge solutions to live full and productive lives, free from daily physical and emotional pain or suffering.

Why is rare disease research important?

    • Over 7,000 rare diseases have been identified. Out of these, 600+ are currently in gene therapy trials. Our mission is to put the focus on NF2 and convince leading labs to run NF2 gene therapy trials.
    • While each disease on its own is rare, 1 in 10 people are living with a rare disease. Every treatment that is developed helps to pave the way for other treatments.
  • Many cancers and benign tumors show mutations in the NF2 gene. A therapy for NF2 may also help in treatment of those cancers and disorders.  In addition to curing NF2, help us cure sporadic vestibular schwannomas (formerly known as acoustic neuromas), meningiomas, breast cancer, prostate cancer, colo-rectal cancer, mesothelioma, and many others.

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Support NF2 BioSolutions and buy merchandise, t-shirts, cups and other items here. Fifty percent of the sales price is donated to NF2 BioSolutions.

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NF2 BioSolutions (Tax-ID 83-0940046) is a Pennsylvania nonprofit public charity.  The U.S. Internal Revenue Service has approved Federal tax-exempt status under Section 501(c)(3).
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